Disease

Gangliosidosis

About the Disease
Gangliosidosis, also known as gangliosidoses, is related to gm1-gangliosidosis, type i and gm1-gangliosidosis, type iii. An important gene associated with Gangliosidosis is HEXA (Hexosaminidase Subunit Alpha), and among its related pathways/superpathways are Metabolism and Glycosaminoglycan metabolism. The drugs Miglustat and Anti-Infective Agents have been mentioned in the context of this disorder. Affiliated tissues include bone marrow, brain and bone, and related phenotypes are no effect and no effect

Common Targets
PHKB | GLB1

疾病靶点研报
Gangliosidosis

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