Disease

Juvenile Amyotrophic Lateral Sclerosis

About the Disease
Juvenile Amyotrophic Lateral Sclerosis, also known as juvenile lou gehrig disease, is related to amyotrophic lateral sclerosis 4, juvenile and amyotrophic lateral sclerosis 2, juvenile. An important gene associated with Juvenile Amyotrophic Lateral Sclerosis is ALS2 (Alsin Rho Guanine Nucleotide Exchange Factor ALS2). Affiliated tissues include cerebellum, skeletal muscle and liver, and related phenotypes are lower limb spasticity and distal amyotrophy

Common Targets
TARDBP | SPG11 | CLEC4C | SPTLC1 | FUS | VRK1 | SETX

疾病靶点研报
Juvenile Amyotrophic Lateral Sclerosis

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