Disease

Medium-chain Acyl-CoA Dehydrogenase Deficiency

About the Disease
Medium-Chain Acyl-Coenzyme a Dehydrogenase Deficiency, also known as medium-chain acyl-coa dehydrogenase deficiency, is related to acyl-coa dehydrogenase, medium-chain, deficiency of and myotonia congenita, autosomal dominant, and has symptoms including lethargy, seizures and vomiting. An important gene associated with Medium-Chain Acyl-Coenzyme a Dehydrogenase Deficiency is ACADM (Acyl-CoA Dehydrogenase Medium Chain). The drugs Glycerin and Protective Agents have been mentioned in the context of this disorder. Affiliated tissues include liver, brain and whole blood.

Common Targets
ACADM

疾病靶点研报
Medium-chain Acyl-CoA Dehydrogenase Deficiency

Note: If you'd like to get a target analysis report for Medium-chain Acyl-CoA Dehydrogenase Deficiency, or if you are interested to learn how our AI-powered BDE-Chem can design therapeutic molecules to interact with the target(s) above against the disease of Medium-chain Acyl-CoA Dehydrogenase Deficiency at a cost 90% lower than traditional approaches, please feel free to contact us at BD@silexon.ai.

Other Diseases

Bronchiolitis | Sponastrime Dysplasia | Charcot-Marie-Tooth Disease Type 4D | Chondrosarcoma | Cholestasis, Intrahepatic | Angiosarcoma | Stiff-man Syndrome | Cutaneous Mastocytosis | Myosin Storage Myopathy | Polyomavirus Nephropathy | Charcot-Marie-Tooth Disease, Type 1A | Parapsoriasis | Mandibuloacral Dysplasia With Type A Lipodystrophy | Hypertension | Hyperparathyroidism-jaw Tumor Syndrome | Central Retinal Artery Occlusion | Neurotoxicity | Schistosomiasis | LRBA Deficiency | Hyperuricemia | Hyperglycemia | Atrial Septal Defect | Delirium | Gerodermia Osteodysplastica | Atelosteogenesis Type 1 | Dyslipidemia | Retinitis Pigmentosa | Retinitis | Hepatitis A | Aromatic L-amino Acid Decarboxylase Deficiency | Borjeson-Forssman-Lehmann Syndrome | Mast Cell Leukemia | Papillon-Lefevre Syndrome | Schaaf-Yang Syndrome | Porphyria, Variegate | Pupil Disorders | Polymyositis | Chitayat Syndrome | Familial Partial Lipodystrophy | Pleural Tuberculosis | Benign Recurrent Intrahepatic Cholestasis 1 | Neonatal Progeroid Syndrome | Bardet-Biedl Syndrome | Congenital Hemolytic Anemia | Wieacker-Wolff Syndrome | Cerebellar Ataxia, Cayman Type | Cardiac Sarcoidosis | Botulism | Arthrogryposis | Scleroderma | Renal Oncocytoma | Hypophosphatasia | Seminoma | Thanatophoric Dysplasia | Platelet Disorders | Congenital Stromal Corneal Dystrophy | Angina Pectoris | Cerebral Cavernous Malformations | Corneal Dystrophies, Hereditary | Biotinidase Deficiency | Acromicric Dysplasia | Patent Foramen Ovale | Hypertelorism | Aneurysm, Abdominal Aortic | Oculopharyngeal Muscular Dystrophy | Inborn Errors Of Metabolism | Angioedema, Acquired | Alpha-mannosidosis | IgA Deficiency | Jaundice, Obstructive | Hermansky-Pudlak Syndrome | Argininosuccinic Aciduria | Malignant Fibrous Histiocytoma | Coffin-Siris Syndrome | Ophthalmoplegia | Compartment Syndrome | Familial Digital Arthropathy-brachydactyly | Pityriasis Rubra Pilaris | Pulmonary Capillary Hemangiomatosis | Postpoliomyelitis Syndrome | Narcolepsy | 3C Syndrome | Sarcoma, Alveolar Soft Part | Anencephaly | Syndactyly | Sitosterolemia | Sick Sinus Syndrome 1 | NDH Syndrome | Nemaline Myopathy 8 | Duchenne Muscular Dystrophy | Alopecia | Mitochondrial DNA Depletion Syndrome 13 | Communication Disorders | Persistent Truncus Arteriosus | Cardiomyopathy, Hypertrophic | Pemphigoid | Rhabdomyosarcoma | Nephropathy | Primary Hyperoxaluria Type 3 | Urofacial Syndrome | Proctitis | Leber Hereditary Optic Neuropathy | Carpal Tunnel Syndrome | Vasculitis | Prostatitis | Cold-induced Sweating Syndrome | Beta-Propeller Protein-associated Neurodegeneration | T-cell Lymphoma, Subcutaneous Panniculitis-like | Multicystic Renal Dysplasia | Alazami Syndrome | Gitelman Syndrome | Neuronal Ceroid Lipofuscinosis | Iron Overload | Craniopharyngioma | Adenomyosis | Lymphoma, Mantle Cell | Lymphoproliferative Disorders | Craniofrontonasal Syndrome | Onchocerciasis | Periodontitis | SAPHO Syndrome | Eosinophilia | Ectrodactyly | Pycnodysostosis | Cornelia De Lange Syndrome | Hypertension, Renovascular | Stroke, Hemorrhagic | Ectopia Lentis, Isolated, Autosomal Recessive | Placenta Previa | Lymphedema | Primary Biliary Cholangitis | 17-beta-hydroxysteroid Dehydrogenase X Deficiency | Toxic Epidermal Necrolysis | Gastric Atrophy | Woodhouse-Sakati Syndrome | Arteriovenous Malformations | Cirrhosis | Hepatitis, Chronic | Localized Scleroderma | Epidermolysis Bullosa Simplex, Dowling-Meara Type | Cerebrotendinous Xanthomatosis | Usher Syndrome Type II | Glioblastoma Multiforme | Mesothelioma, Malignant | Osteonecrosis Of The Jaw | Crimean-Congo Hemorrhagic Fever | Blepharitis | Macular Corneal Dystrophy Type 1 | Mucormycosis | Smith-Kingsmore Syndrome | Transient Bullous Dermolysis Of The Newborn | Pyruvate Dehydrogenase Deficiency | Colitis | Delayed Sleep Phase Syndrome | TARP Syndrome | Achromatopsia | Retinal Diseases | Congenital Disorders Of Glycosylation | HELLP Syndrome | Melanocytic Nevus | Viral Meningitis | Optic Neuritis | Encephalopathy | Potocki-Shaffer Syndrome | Pilomatrix Carcinoma | Multisystemic Smooth Muscle Dysfunction Syndrome | Mitochondrial DNA Depletion Syndrome, Myopathic Form | Pyloric Stenosis, Infantile Hypertrophic | Lennox-Gastaut Syndrome | Congenital Heart Block | X-linked Creatine Transporter Deficiency | Retinal Vasculitis | Autosomal Recessive Bestrophinopathy | Osteogenesis Imperfecta Type II | Nutrition Disorders | Congenital Disorders Of Glycosylation Type II | Ileitis | Choriocarcinoma | Bronchitis, Chronic | Myocardial Infarction | Dupuytren Disease | Progressive Familial Intrahepatic Cholestasis Type 2 | Endometriosis | Chronic Mucocutaneous Candidiasis | Congenital Heart Defects | Johanson-Blizzard Syndrome | Peeling Skin Syndrome, Acral Type | Pneumothorax | Amelogenesis Imperfecta | Intestinal Obstruction | Intestinal Hypomagnesemia 1 | Pemphigus Vulgaris | Osteochondroma | Cartilage Disorders | Sarcoma | Osteogenesis Imperfecta Type I | Adenomatoid Tumor | Genitopatellar Syndrome | Hemolytic Uremic Syndrome | Farber Disease | Waldenstrom Macroglobulinemia | Neurofibromatosis Type 2 | Knobloch Syndrome | Plasma Cell Dyscrasia | 3-methylglutaconic Aciduria Type IV | Gangliosidosis, GM1 | Ataxia-ocular Apraxia 2 | Seasonal Mood Disorder | Uveitis, Anterior | Spermatocele | Hyperinsulinemic Hypoglycemia | Ameloblastic Carcinoma | Exotropia | Kawasaki Disease | Hemangioendothelioma | Melanoma, Uveal | Membranous Nephropathy | Brooke-Spiegler Syndrome | Carcinoid Tumor | 3-methylglutaconic Aciduria Type I | Congenital Nephrotic Syndrome | Acne | Cholangiocarcinoma | Pulmonary Tuberculosis | VEXAS Syndrome | Diabetes | Creatine Deficiency Syndrome Due To AGAT Deficiency | Frontotemporal Dementia With Amyotrophic Lateral Sclerosis | Poikiloderma With Neutropenia | Dowling-Degos Disease | Congenital Dysfibrinogenemia | Usher Syndrome | Sick Sinus Syndrome | Chordoid Glioma | Cholesteryl Ester Storage Disease | Primary Sclerosing Cholangitis | Liver Failure, Acute Infantile | Hereditary Multiple Exostoses | Plasma Cell Leukemia | Osteochondrosis | Oculocutaneous Albinism Type 4 | Hypophosphatemic Rickets With Hypercalciuria, Hereditary | Iron Metabolism Disorders | Paronychia | Mevalonate Kinase Deficiency | Neurofibroma | Hyperandrogenemia | Pulmonary Sclerosing Hemangioma | Glutaric Aciduria Type 3 | Osteoarthritis | Ulcerative Colitis | Thyroid Dysgenesis | Necrotizing Autoimmune Myopathy | Asperger Syndrome | Congenital Lipoid Adrenal Hyperplasia | Spinocerebellar Ataxia Type 16 | Kaposi Sarcoma | Chronic Lymphocytic Leukemia | Bullous Pemphigoid | Nijmegen Breakage Syndrome | Renal Failure | Frank-ter Haar Syndrome | Uveitis | Cryoglobulinemia | Kaposiform Hemangioendothelioma | Chronic Thromboembolic Pulmonary Hypertension | Multicentric Carpotarsal Osteolysis Syndrome | Craniofacial Dysostosis | Angiosarcoma Of The Breast | Chloridorrhea, Congenital | Early Infantile Epileptic Encephalopathy | Primary Lateral Sclerosis | Leiomyoma | Hereditary Sensory Neuropathy Type 1 | Multifocal Motor Neuropathy | Primary Aldosteronism | Phenylketonuria II | Pseudoachondroplasia | Congenital Dyserythropoietic Anemia | Hypomyelination With Atrophy Of Basal Ganglia And Cerebellum | Thromboembolism | Nager Acrofacial Dysostosis | Aspergillosis | Hemolytic Anemia | Purpura | Inflammatory Myopathy | Myelodysplasia | Intellectual Disability, Autosomal Dominant 5 | Cryopyrin-associated Periodic Syndromes | Renal Tubular Acidosis | KBG Syndrome | Vitamin K Deficiency | Blood Protein Disorders | Osteoglophonic Dysplasia | Overactive Bladder | Frontometaphyseal Dysplasia | Acrodysostosis | Amyloidosis | Glycogen Storage Disease Type 5 | Hepatoblastoma | Extramammary Paget's Disease | Adenoid Cystic Carcinoma | Netherton Syndrome | Adenocarcinoma | Iron Deficiency Anemia | Amish Infantile Epilepsy Syndrome | Alkaptonuria | Hepatitis D | Heimler Syndrome | Pancytopenia | Polycystic Ovary Syndrome | Thrombophlebitis | Osteopathia Striata With Cranial Sclerosis | Polymyalgia Rheumatica | Sengers Syndrome | Hypertensive Retinopathy | Anxiety Disorders | Thin Basement Membrane Disease | Cole-Carpenter Syndrome | Dental Caries | Episodic Ataxia Type 1 | Renal-hepatic-pancreatic Dysplasia | Schizencephaly | Branchiootorenal Syndrome | Chylomicron Retention Disease | Encephalopathy, Hepatic | Congestive Heart Failure | Skin Fragility-woolly Hair Syndrome | Rhabdoid Tumor | Cerebellofaciodental Syndrome | Schwartz-Jampel-Aberfeld Syndrome | 3-M Syndrome | Poretti-Boltshauser Syndrome | Distal Myopathy | Sialidosis Type I | Phenylketonuria | Scleroderma, Diffuse | HANAC Syndrome | Lymphoma, AIDS-related | Gilbert Syndrome | Pelvic Inflammatory Disease | Phosphoenolpyruvate Carboxykinase Deficiency, Cytosolic | Retinitis Pigmentosa 3 | Atherosclerosis | Diabetes Gestational | Fraser Syndrome | Sarcomatoid Carcinoma Of The Lung | Blomstrand Osteochondrodysplasia | Paternal Uniparental Disomy Of Chromosome 14 | Hyperphosphatasia With Intellectual Disability Syndrome 4 | Takotsubo Cardiomyopathy | Light Chain Amyloidosis | Hypertriglyceridemia | Pulmonary Alveolar Microlithiasis | Hypoglycemia | Stargardt Disease | Chronic Idiopathic Myelofibrosis | Familial Thoracic Aortic Aneurysm | Charcot-Marie-Tooth Disease Axonal Type 2N | Neurofibrosarcoma | Eczema | Glutathione Synthetase Deficiency | Spinocerebellar Ataxia Type 13 | Silicosis | Trichothiodystrophy | Porokeratosis | Giant Cell Glioblastoma | Sleep Apnea, Obstructive | Motor Neuron Diseases | Tangier Disease | Fanconi Syndrome | Osteoporosis, Postmenopausal | Neuroma | Primary Hyperoxaluria | Hypermethioninemia | Restrictive Dermopathy | Hyperbilirubinemia | Evans Syndrome | Rash | Craniolenticulosutural Dysplasia | Schamberg Disease | Osteoporosis | Hemorrhagic Disorders | Scleritis | Colitis, Collagenous | Feingold Syndrome | Desmosterolosis | Cellulitis | Angiomyolipoma | Stuttering | Acrodermatitis | Waardenburg Syndrome Type 4A | Familial Isolated Hyperparathyroidism | Riboflavin Transporter Deficiency Neuronopathy | Lung Diseases | Synovitis | Neurocutaneous Melanocytosis | Blue Rubber Bleb Nevus Syndrome | POEMS Syndrome | Martsolf Syndrome